GENE THERAPY Definition & Meaning

gene therapy

noun

Medicine/Medical.

the application of genetic engineering to the transplantation of genes into human cells in order to cure a disease caused by a genetic defect, as a missing enzyme.

gene therapy

noun

the replacement or alteration of defective genes in order to prevent the occurrence of such inherited diseases as haemophilia. Effected by genetic engineering techniques, it is still at the experimental stage

gene therapy

The treatment of a disorder or disease, especially one caused by the inheritance of a defective gene, by replacing defective genes with healthy ones through genetic engineering.

gene therapy

A promising technology that involves replacing a defective gene in the body with a healthy one. This can be done by removing cells from the body, using genetic engineering techniques to change defective sequences in the DNA, and then reinserting the cells. This technique has been carried out successfully, for example, on bone marrow cells, in which defective cells were successfully replaced with healthy, genetically engineered cells. Scientists hope to find an agent, such as a therapeutic virus , that will be able to correct defective DNA in situ . ( See cloning vector .)

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�y��vlog History and Origins

Origin of gene therapy¹

First recorded in 1970–75

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Example Sentences

Examples have not been reviewed.

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain "life-changing improvements" to their sight, according to doctors at Moorfields Eye Hospital in London.

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Gene therapy for another form of genetic blindness has been available on the NHS since 2020.

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Jace, from Conneticut in the United States, had the gene therapy in London when he was just two years old.

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Drug companies sponsored only 40% of the U.S. gene therapy trials active in January 2019, according to a study Sarpatwari co-authored.

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Once Novartis acquired AveXis, it turned to setting a price for its much-anticipated gene therapy.

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